Glycogen storage disease type I
RecruitingStudy on Long-Term Safety and Pregnancy Outcomes of Pariglasgene Brecaparvovec in Patients with Glycogen Storage Disease Type Ia (GSDIa)
Study on Long-Term Safety and Pregnancy Outcomes of Pariglasgene Brecaparvovec in Patients with Glycogen Storage Disease Type Ia (GSDIa)
- Disease:Glycogen storage disease type I
- Substances:Pariglasgene Brecaparvovec
Denmark- Participants:0–17 years · 18–64 years · 65+ years
- Substances:Pariglasgene Brecaparvovec
- Sponsor:Ultragenyx Pharmaceutical Inc.











