Factor IX deficiency
RecruitingStudy on the Safety and Effectiveness of REGV131 and LNP1265 for Adults with Hemophilia B
Study on the Safety and Effectiveness of REGV131 and LNP1265 for Adults with Hemophilia B
- Disease:Factor IX deficiency
- Substances:Adeno-Associated Virus Vector Serotype 8 Containing The Human F9 GeneMessenger Rna Encoding Cas9+1
Italy- Participants:18–64 years · 65+ years
- Substances:Adeno-Associated Virus Vector Serotype 8 Containing The Human F9 Gene
- Sponsor:Regeneron Pharmaceuticals Inc.










