Rare diseases
Investigational molecules
Locations
Study of the effects of Ibutamoren Mesilate in prepubertal children with growth hormone deficiency
FranceStudy of dexmedetomidine versus placebo to reduce opioid use in premature babies requiring mechanical ventilation for respiratory distress
FranceComparison of intrathecal baclofen pump and selective dorsal rhizotomy for children with cerebral palsy who cannot walk
BelgiumTesting the safety and effectiveness of stem cells from fat tissue in children with autism spectrum disorder and digestive problems
Denmark
ItalyStudy of ASP2957 Gene Therapy for Male Patients with X-linked Myotubular Myopathy Who Require Breathing Support with Ventilators
FranceStudy of sodium butyrate enemas for bowel function recovery after surgery in children and adults with Hirschsprung's disease
FranceA Study of Blinatumomab in Children with Relapsed or Treatment-Resistant B Cell Acute Lymphoblastic Leukemia with Remaining Disease Traces
FranceA Study of Migalastat Safety and Effects in Children Aged 2 to 12 Years with Fabry Disease and Suitable Gene Changes
BelgiumStudy of aldesleukin in children aged 4 to 6 years with autism spectrum disorder whose mothers had immune system activation during pregnancy
FranceA Study of Intranasal Dexmedetomidine for Sedation in Children Undergoing Non-Invasive Radiological Procedures
BelgiumA Study Comparing Tacrolimus and Ciclosporin Eye Drops for Children and Adults with Moderate to Severe Vernal Keratoconjunctivitis
BulgariaClinical research plays a vital role in developing safe and effective treatments for younger patients. Pediatric clinical trials are trials designed specifically for infants, children, and adolescents. They help researchers understand how new therapies, vaccines, or medical procedures work in younger populations and ensure that treatments are safe and appropriate for their age group.
Children are not simply smaller versions of adults. Their bodies grow and develop, which means medications may work differently than they do in adults. For this reason, therapies must be carefully studied in pediatric populations.
Another important reason for pediatric clinical trials is that some diseases occur primarily or exclusively in children. Certain genetic conditions, developmental disorders, and rare pediatric diseases affect only young patients. Without dedicated research involving children and adolescents, it would be difficult to develop treatments specifically designed for these conditions.
Pediatric research also helps doctors determine:
Participants in pediatric clinical trials may include infants, children, and teenagers depending on the trial design. Each trial has specific eligibility criteria based on age, health condition, and medical history.
Because participants are minors, the process always involves:
This ensures that families fully understand the purpose of the research, the procedures involved, and any potential risks or benefits.
Safety is the highest priority in pediatric clinical trials. These trials follow strict ethical and regulatory standards in Europe and internationally. Research protocols are reviewed by ethics committees and regulatory authorities to ensure that the risks are minimized and justified by the potential benefits of the research.
Children participating in clinical trials are monitored closely by qualified healthcare professionals throughout the entire process. Families receive detailed information about trial procedures, medical monitoring, and the right to withdraw from the trial at any time.
Our search platform allows parents and guardians to explore pediatric clinical trials available in different regions. Using the search tool, families can find trials based on factors such as age group, medical condition, and location.
Clinical trials for children and adolescents are essential for advancing pediatric medicine. By participating in research, families contribute to the development of safer and more effective treatments for young patients today and in the future.
Tell us about your condition – we search every trial in Europe and connect you with the right site.
