Anaemia
Not yet recruitingEffect of mitapivat versus placebo on transfusion burden in patients with sickle cell disease
Belgium- Participants:0–17 years · 18–64 years · 65+ years
- Substances:Mitapivat
- Sponsor:Agios Pharmaceuticals Inc.
Rare diseases
Investigational molecules
Locations

88 Sidney Street, 02139-4137, United States
The sponsor demonstrates significant commitment to advancing treatment options for patients with acute myeloid leukemia and myelodysplastic syndromes. Research initiatives focus on addressing relapsed or refractory disease in adult populations, with particular attention to patients who have exhausted standard therapeutic options. The investigational approaches target specific molecular pathways involved in hematologic malignancies, exploring novel mechanisms that may offer clinical benefit to patients with limited treatment alternatives.
The research portfolio includes trials designed to evaluate therapeutic efficacy in patients who have previously received multiple lines of therapy, addressing a critical unmet need in refractory hematologic conditions.
Agios Pharmaceuticals Inc. runs clinical trials in conditions such as Thalassaemia, Anaemia, Thalassaemia beta, Thalassaemia alpha, among others.
Clinical trials registered by this sponsor – none is enrolling right now.
Belgium
Greece
Greece
Belgium
Bulgaria
Bulgaria
Czechia
Belgium
France
France
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