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PTC Therapeutics Inc.
Sponsor

PTC Therapeutics Inc.

United States 500 Warren Corporate Center Drive, 07059, United States

About the sponsor

PTC Therapeutics Inc. supports clinical research in amyotrophic lateral sclerosis and Huntington’s disease, with attention to disease progression, neurological function, and biomarker changes linked to central nervous system involvement.

  • Amyotrophic lateral sclerosis
  • Huntington’s disease
  • Huntingtin protein biomarkers

These studies reflect a focus on conditions with progressive motor and cognitive decline.

About Specializations

PTC Therapeutics Inc. runs clinical trials in conditions such as Phenylketonuria, Friedreich's ataxia, Neoplasm, Autoimmune disorder, among others.

Recruiting now

Ongoing trials

Clinical trials run by this sponsor – those enrolling participants first.

Condition
Country
City
Type of trial
Recruitment status
Quick filters

9 clinical trials

Phenylketonuria

Recruiting
Registered drugNo placebo
Countries:FranceFrance
  • Participants:0–17 years
  • Substances:Sepiapterin
  • Sponsor:PTC Therapeutics Inc.

Friedreich's ataxia

Recruiting
InvestigationalNo placebo
Countries:FranceFrance
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:Vatiquinone
  • Sponsor:PTC Therapeutics Inc.

Neoplasm

Not recruiting
InvestigationalNo placebo
Countries:HungaryHungary
  • Participants:18–64 years · 65+ years
  • Sponsor:PTC Therapeutics Inc.

Autoimmune disorder

Not recruiting
Investigational
Countries:The NetherlandsThe Netherlands
  • Participants:18–64 years · Healthy volunteers
  • Sponsor:PTC Therapeutics Inc.

Fabry's disease

Not recruiting
InvestigationalNo placebo
Countries:GermanyGermany
  • Participants:18–64 years · 65+ years
  • Substances:Isaralgagene Civaparvovec
  • Sponsor:PTC Therapeutics Inc.

Phenylketonuria

Not recruiting
InvestigationalNo placebo
Countries:CzechiaCzechia
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:(S)-2-Amino-6-(2-Hydroxypropanoyl)-7,8-Dihydropteridin-4(3H)-One
  • Sponsor:PTC Therapeutics Inc.

Amyotrophic lateral sclerosis

Not recruiting
Investigational
Countries:BelgiumBelgium
  • Participants:18–64 years · 65+ years
  • Substances:Utreloxastat
  • Sponsor:PTC Therapeutics Inc.

Phenylketonuria

Not recruiting
Registered drugNo placebo
Countries:CzechiaCzechia
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:(S)-2-Amino-6-(2-Hydroxypropanoyl)-7,8-Dihydropteridin-4(3H)-One
  • Sponsor:PTC Therapeutics Inc.

Huntington's disease

Not recruiting
Investigational
Countries:AustriaAustria
  • Participants:18–64 years · 65+ years
  • Substances:Ptc518
  • Sponsor:PTC Therapeutics Inc.

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