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Rare disease

Alpha-1 antitrypsin deficiency

  • 11 clinical trials
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11 Clinical trials

Countries:DenmarkDenmark
  • Participants:18–64 years · 65+ years
  • Substances:Human Alpha1-Proteinase Inhibitor
  • Sponsor:CSL Behring LLC
Countries:DenmarkDenmark
  • Participants:18–64 years · 65+ years
  • Substances:Human Alpha1-Proteinase Inhibitor
  • Sponsor:Grifols Therapeutics LLC
Countries:GermanyGermany
  • Participants:18–64 years · 65+ years
  • Substances:Human Alpha1-Proteinase Inhibitor
  • Sponsor:Grifols S.A.
Countries:IrelandIreland
  • Participants:18–64 years
  • Substances:Gr0015
  • Sponsor:Beam Therapeutics Inc.
Registered drug
Countries:AustriaAustria
  • Participants:18–64 years · 65+ years
  • Substances:Fazirsiran
  • Sponsor:Takeda Development Center Americas Inc.
Countries:AustriaAustria
  • Participants:18–64 years · 65+ years
  • Substances:Fazirsiran
  • Sponsor:Takeda Development Center Americas Inc.
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