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Rare disease

Angelman's syndrome

  • 6 clinical trials
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6 Clinical trials

Countries:GermanyGermany
  • Participants:0–17 years · 18–64 years
  • Substances:2'-O-(2-Methoxyethyl) Modified Antisense Oligonucleotide Targeting Ube3A Antisense Transcript Rna
  • Sponsor:Ionis Pharmaceuticals Inc.
Countries:FranceFrance
  • Participants:0–17 years · 18–64 years
  • Substances:2'-O-(2-Methoxyethyl) Modified Antisense Oligonucleotide Targeting Ube3A Antisense Transcript Rna
  • Sponsor:Ionis Pharmaceuticals Inc.
Countries:FranceFrance
  • Participants:0–17 years · 18–64 years
  • Substances:APAZUNERSEN
  • Sponsor:Ultragenyx Pharmaceutical Inc.
Countries:GermanyGermany
  • Participants:0–17 years
  • Substances:APAZUNERSEN
  • Sponsor:Ultragenyx Pharmaceutical Inc.
Countries:FranceFrance
  • Participants:0–17 years
  • Substances:APAZUNERSEN
  • Sponsor:Ultragenyx Pharmaceutical Inc.
Countries:ItalyItaly
  • Participants:0–17 years
  • Substances:Rugonersen
  • Sponsor:F. Hoffmann-La Roche AG
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