Recruiting
Angelman's syndrome
RecruitingInvestigationalNo placebo
A Phase 3 study to evaluate the efficacy and safety of ION582 in children and adults with Angelman syndrome
InvestigationalNo placebo
- Disease:Angelman's syndrome
- Substances:2'-O-(2-Methoxyethyl) Modified Antisense Oligonucleotide Targeting Ube3A Antisense Transcript Rna
Countries:
Germany
Germany- Participants:0–17 years · 18–64 years
- Substances:2'-O-(2-Methoxyethyl) Modified Antisense Oligonucleotide Targeting Ube3A Antisense Transcript Rna
- Sponsor:Ionis Pharmaceuticals Inc.






