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Rare disease

Duchenne muscular dystrophy

  • 28 clinical trials
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28 Clinical trials

Countries:BelgiumBelgium
  • Participants:0–17 years · 18–64 years
  • Sponsor:Entrada Therapeutics Inc.
Countries:BelgiumBelgium
  • Participants:0–17 years
  • Sponsor:Avidity Biosciences Inc.
Countries:ItalyItaly
  • Participants:0–17 years · 18–64 years
  • Sponsor:Biomarin Pharmaceutical Inc.
Countries:BelgiumBelgium
  • Participants:0–17 years · 18–64 years
  • Substances:Sodium Chloride
  • Sponsor:Entrada Therapeutics Inc.
Countries:BelgiumBelgium
  • Participants:0–17 years · 18–64 years
  • Substances:Sodium Chloride
  • Sponsor:Entrada Therapeutics Inc.
Countries:ItalyItaly
  • Participants:0–17 years
  • Substances:SGT-003
  • Sponsor:Solid Biosciences Inc.
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