Not recruiting
Leukocyte adhesion deficiency+1
Not recruitingInvestigationalNo placebo
Study on Long-Term Safety and Efficacy of Gene Therapy for Leukocyte Adhesion Deficiency-I Using RP-L201 in Patients with LAD-I
InvestigationalNo placebo
- Disease:Leukocyte adhesion deficiencyLeukocyte adhesion deficiency type I
- Substances:Autologous Cd34+ Haematopoietic Stem Cells Genetically Modified With Lentiviral Vector Encoding The Cd18 Gene
Countries:
Spain
Spain- Participants:0–17 years · 18–64 years
- Substances:Autologous Cd34+ Haematopoietic Stem Cells Genetically Modified With Lentiviral Vector Encoding The Cd18 Gene
- Sponsor:Rocket Pharmaceuticals Inc.