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Rare disease

Niemann-Pick disease

  • 3 clinical trials
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3 Clinical trials

Countries:FranceFrance
  • Participants:0–17 years · 18–64 years
  • Sponsor:Sanofi Winthrop Industrie
Countries:SpainSpain
  • Participants:18–64 years
  • Substances:Aprepitant
  • Sponsor:Bellvitge University Hospital

Niemann-Pick disease

Not recruiting
Registered drug
Countries:GermanyGermany
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:Hydroxypropylbetadex
  • Sponsor:Cyclo Therapeutics Inc.
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