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Rare disease

Paroxysmal nocturnal haemoglobinuria

  • 15 clinical trials
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15 Clinical trials

Countries:FranceFrance
  • Participants:0–17 years
  • Substances:Iptacopan Hydrochloride
  • Sponsor:Novartis Pharma AG
Countries:The NetherlandsThe Netherlands
  • Participants:18–64 years · 65+ years
  • Substances:Ravulizumab
  • Sponsor:Stichting Radboud universitair medisch centrum
Countries:FranceFrance
  • Participants:0–17 years
  • Substances:Danicopan
  • Sponsor:Alexion Pharmaceuticals Inc.
Countries:The NetherlandsThe Netherlands
  • Participants:0–17 years
  • Substances:Pegcetacoplan
  • Sponsor:Apellis Pharmaceuticals Inc.
Countries:ItalyItaly
  • Participants:18–64 years · 65+ years
  • Substances:Cemdisiran
  • Sponsor:Regeneron Pharmaceuticals Inc.
Countries:FranceFrance
  • Participants:18–64 years · 65+ years · Healthy volunteers
  • Substances:Crovalimab
  • Sponsor:F. Hoffmann-La Roche AG
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