Recruiting
Propionic acidaemia
RecruitingInvestigationalNo placebo
A study to evaluate the long-term safety and effectiveness of mRNA-3927 in patients with Propionic Acidemia
InvestigationalNo placebo
- Disease:Propionic acidaemia
- Substances:Modified Messenger Ribonucleic Acid Encoding Human Propionyl-Coenzyme A Carboxylase Alpha And Beta Subunits Encapsulated Into Lipid Nanoparticles
Countries:
France
France- Participants:0–17 years · 18–64 years
- Substances:Modified Messenger Ribonucleic Acid Encoding Human Propionyl-Coenzyme A Carboxylase Alpha And Beta Subunits Encapsulated Into Lipid Nanoparticles
- Sponsor:Moderna Therapeutics Inc.



