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Rare disease

Stargardt's disease

  • 6 clinical trials
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6 Clinical trials

Countries:BelgiumBelgium
  • Participants:0–17 years · 18–64 years
  • Substances:Tinlarebant
  • Sponsor:Belite Bio Inc.
Countries:BelgiumBelgium
  • Participants:18–64 years
  • Substances:ADENO-ASSOCIATED VIRUS VECTOR SEROTYPE 8 ENCODING THE ABCA4 PROTEIN, C-REGION
  • Sponsor:Splicebio S.L.
Countries:BelgiumBelgium
  • Participants:0–17 years · 18–64 years
Countries:BelgiumBelgium
  • Participants:0–17 years · 18–64 years
  • Sponsor:Aavantgarde Bio S.r.l.
Countries:FranceFrance
  • Participants:0–17 years · 18–64 years
  • Substances:Lentiviral Vector Containing The Human Abca4 Gene
  • Sponsor:Sanofi-Aventis Recherche & Developpement

Stargardt's disease

Not recruiting
Investigational
Countries:BelgiumBelgium
  • Participants:0–17 years · 18–64 years
  • Substances:Tinlarebant
  • Sponsor:Belite Bio Inc.
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