Rare diseases
Investigational molecules
Locations
237 conditions with trials, the busiest first
741 trials across Europe, recruiting first
Study on the Effectiveness and Safety of Vosoritide for Children with Hypochondroplasia
FranceStudy of Intrathecal Cebsulfase Alfa for Children with Late Infantile Metachromatic Leukodystrophy
BelgiumStudy on Long-Term Safety of INBRX-101 for Adults with Alpha-1 Antitrypsin Deficiency Emphysema
DenmarkStudy on the Effects of Paltusotine for Patients with Untreated Acromegaly
BulgariaStudy on Testosterone Undecanoate for Muscle Strength and Mass in Men with Obesity and Low Testosterone Undergoing Bariatric Surgery
DenmarkStudy on Treating Acute Gout Attacks with Prednisolone and Colchicine for Primary Care Patients
GermanyStudy Comparing Retatrutide and Tirzepatide for Weight Loss in Adults with Obesity
GermanyStudy on the Safety and Effects of VX-264 for Patients with Type 1 Diabetes
GermanyEvaluation of fenofibrate treatment on beta cell function in children and adolescents newly diagnosed with type 1 diabetes
PolandStudy of Bempedoic Acid for Children Aged 6-17 with Familial Hypercholesterolemia
DenmarkStudy of Efgartigimod PH20 SC for Adults with Thyroid Eye Disease
AustriaStudy on Plozasiran and ARO-APOC3 for Adults with Severe Hypertriglyceridemia
BulgariaThe therapies tested most often in Metabolism and nutrition disorders trials.
Tell us about your condition – we search every trial in Europe and connect you with the right site.
