Rare diseases
Investigational molecules
Locations
453 conditions with trials, the busiest first
1 389 trials across Europe, recruiting first
Study on Efgartigimod IV for Adults with Seronegative Generalized Myasthenia Gravis
BelgiumStudy on Long-Term Safety and Efficacy of Cebsulfase Alfa for Children with Late Metachromatic Leukodystrophy Receiving Intrathecal Enzyme Replacement
CzechiaStudy on Testosterone Undecanoate for Neuroprotection and Myelin Repair in Patients with Relapsing Remitting Multiple Sclerosis
FranceStudy on the Effectiveness of Fremanezumab for Preventing Migraines in Children and Teens Aged 6 to 17
FinlandStudy on the Effects of Vidofludimus Calcium in Adults with Relapsing Multiple Sclerosis
EstoniaStudy on Long-Term Safety and Effectiveness of Vamorolone in Boys with Duchenne Muscular Dystrophy Who Completed Previous Vamorolone Studies
BelgiumStudy on Glenzocimab for Patients with Acute Ischemic Stroke Undergoing Mechanical Thrombectomy
FranceStudy on the Safety and Tolerability of Leriglitazone for Children with Rett Syndrome
SpainStudy of tovorafenib versus standard chemotherapy as first treatment for children with low-grade glioma with RAF gene changes
AustriaStudy on Migraine: Effects of Fremanezumab on Brain Chemistry in Patients with and without Aura
AustriaStudy on Nimodipine for Hearing Preservation in Patients Undergoing Acoustic Schwannoma Surgery
GermanyStudy on the Effects of Bosentan for Patients with Early Stage Non-Arteritic Anterior Ischemic Optic Neuropathy
FranceThe therapies tested most often in Nervous system disorders trials.
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