Paroxysmal nocturnal haemoglobinuria
Not recruitingStudy on the Long-term Safety and Effectiveness of Danicopan with Ravulizumab or Eculizumab for Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH)
Study on the Long-term Safety and Effectiveness of Danicopan with Ravulizumab or Eculizumab for Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH)
- Disease:Paroxysmal nocturnal haemoglobinuria
- Substances:DanicopanEculizumab+1
Czechia- Participants:18–64 years · 65+ years
- Substances:Danicopan
- Sponsor:Alexion Pharmaceuticals Inc.













