Rare diseases
Investigational molecules
Locations
374 conditions with trials, the busiest first
796 trials across Europe, recruiting first
Study on Thymalfasin for Adults with Cystic Fibrosis
ItalyStudy on Eteplirsen for Patients with Duchenne Muscular Dystrophy with Deletion Mutations Amenable to Exon 51 Skipping
CzechiaStudy on Atezolizumab and Tiragolumab for Patients with Head and Neck Cancer, Metastatic Melanoma, and Other Advanced Solid Tumors
The NetherlandsStudy on the Safety of Donidalorsen for Patients with Hereditary Angioedema
The NetherlandsStudy on Long-Term Safety of Oral Lucerastat for Adults with Fabry Disease
AustriaStudy on Dantrolene Sodium for Treating Darier Disease in Affected Patients
SwedenStudy on Mavorixafor for Treating WHIM Syndrome in Patients
DenmarkStudy on the Safety of Allogeneic Adipose Tissue-Derived Mesenchymal Stromal Cells for Patients with Epidermolysis Bullosa
CzechiaStudy on the Effects and Safety of ZYN002 Gel for Children, Adolescents, and Young Adults with Fragile X Syndrome
IrelandStudy of Trastuzumab, Pertuzumab, and Chemotherapy Combination with Response-Guided Treatment for Patients with HER2-Positive Breast Cancer
The NetherlandsStudy of Osimertinib for Patients with EGFR-Mutated Non-Small Cell Lung Cancer
LithuaniaStudy of BDC-1001 and Nivolumab for Patients with Advanced HER2-Positive Solid Tumors
FranceThe therapies tested most often in Congenital, familial and genetic disorders trials.
Tell us about your condition – we search every trial in Europe and connect you with the right site.
